@inproceedings{inproceedings, title = {{AAV-mediated gene editing as a potential therapeutic approach for C9ORF72-linked ALS/FTD}},
url = {{}},
year = {{2019}},
month = {{1}},
author = {{Alves-Cruzeiro J and Karyka E and Bauer C and Coldicott I and Hautbergue G and Webster C and Castelli L and Simon S and Myszczynska M and Ferraiuolo L and Azzouz M}},
volume = {{30}},
journal = {{HUMAN GENE THERAPY}},
issue = {{11}},
pages = {{A96-A96}},
note = {{Accessed on 2025/05/25}}}